FALCONE, GERMANA
FALCONE, GERMANA
Istituto di Biochimica e Biologia Cellulare - IBBC - Sede Secondaria Monterotondo
circARHGAP10 as a candidate biomarker and therapeutic target in myotonic dystrophy type 1
2025 Baci, D.; Tastsoglou, S.; Provenzano, C.; Perfetti, A.; Izzo, M.; Lisanti, M.; Frolova, S.; Voellenkle, C.; Tascini, A. S.; Cardani, R.; Cardinali, B.; Meola, G.; Falcone, G.; Martelli, F.
Muscle‐specific gene editing improves molecular and phenotypic defects in a mouse model of myotonic dystrophy type 1
2025 Izzo, Mariapaola; Battistini, Jonathan; Golini, Elisabetta; Voellenkle, Christine; Provenzano, Claudia; Orsini, Tiziana; Strimpakos, Georgios; Scavizzi, Ferdinando; Raspa, Marcello; Baci, Denisa; Frolova, Svetlana; Tastsoglou, Spyros; Zaccagnini, Germana; Garcia‐manteiga, Jose Manuel; Gourdon, Genevieve; Mandillo, Silvia; Cardinali, Beatrice; Martelli, Fabio; Falcone, Germana
Muscle-specific gene editing improves molecular and phenotypic defects in a mouse model of Myotonic Dystrophy type 1
2024 Izzo, Mariapaola; Battistini, Jonathan; Golini, Elisabetta; Provenzano, Claudia; Orsini, Tiziana; Strimpakos, Georgios; Scavizzi, Ferdinando; Raspa, Marcello; Gourdon, Genevieve; Mandillo, Silvia; Cardinali, Beatrice; Falcone, Germana
Excessive rest time during active phase is reliably detected in a mouse model of myotonic dystrophy type 1 using home cage monitoring
2023 Golini, Elisabetta; Rigamonti, Mara; Raspa, Marcello; Scavizzi, Ferdinando; Falcone, Germana; Gourdon, Genevieve; Mandillo, Silvia
GENE EDITING IN MYOTONIC DYSTROPHY TYPE 1: ASSESSMENT OF EFFICIENCY, SAFETY AND THERAPEUTIC EFFECT OF CTG-REPEAT DELETION IN A MOUSE MODEL OF DISEASE
2023 Izzo Mariapaola ; Battistini J.; Cardinali B.; Provenzano C.; Mandillo S.; Golini E.; Strimpakos G.; Scavizzi F.; Raspa M.; Voellenkle C.; Perfetti A.; Baci D.; Martelli F.; Lazarevic D.; GarciaManteiga J.M.; Gourdon G.; Falcone Germana
Sleep-related phenotypes are non-invasively uncovered using home cage monitoring in mouse models of ALS and DM1
2023 Golini, Elisabetta; Rigamonti, Mara; Iannello, Fabio; Scavizzi, Ferdinando; Raspa, Marcello; Gourdon, Genevieve; Falcone, Germana; Mandillo, Silvia
Study of pathogenetic mechanisms and development of new therapeutic strategies for Myotonic Dystrophy type 1
2023 M. Izzo ; J. Battistini ; B. Cardinali ; C. Provenzano ; S. Mandillo ; E. Golini ; G. Strimpakos ; F. Scavizzi ; M. Raspa ; C. Voellenkle ; D. Baci ; A. Perfetti ; D. Lazarevic ; J. GarciaManteiga ; G. Gourdon ; F. Martelli ; G. Falcone
Application of CRISPR/Cas9 strategy for gene therapy of Myotonic Dystrophy type 1
2022 Falcone, G; Izzo, M; Cardinali, B; Provenzano, C; Battistini, J; Mandillo, S; Golini, E; Strimpakos, G; Scavizzi, F; Mraspa, ; Voellenkle, C; Baci, D; Perfetti, A; Lazarevic, D; Garciamanteiga, J; Gourdon, G; Martelli, F
BEHAVIOURAL ABNORMALITIES IN DMSXL MICE, A MODEL OF MYOTONIC DYSTROPHY TYPE 1
2022 Mandillo, Silvia; Golini, Elisabetta; Orsini, Tiziana; Rigamonti, Mara; Izzo, Mariapaola; Battistini, Jonathan; Cardinali, Beatrice; Provenzano, Claudia; Strimpakos, Georgios; Scavizzi, Ferdinando; Raspa, Marcello; Genevievegourdon, ; Falcone, Germana
Circular RNA role in Myotonic Dystrophy type 1
2022 Baci, D; Perfetti, A; Voellenkle, C; Cardani, R; Meola, G; Tascini, As; Provenzano, C; Cardinali, B; Falcone, G; Fmartelli,
miRNome and Proteome Profiling of Small Extracellular Vesicles Secreted by Human Glioblastoma Cell Lines and Primary Cancer Stem Cells
2022 Cifola, Ingrid; Fratini, Federica; Cardinali, Beatrice; Palmieri, Valentina; Gatti, Giuliana; Selmi, Tommaso; Donzelli, Sara; Sacconi, Andrea; Cesarini, Valeriana; E Marei, Hany; Papi, Massimilano; Blandino, Giovanni; Cenciarelli, Carlo; Falcone, Germana; D'Agnano, Igea
Molecular Therapies for Myotonic Dystrophy Type 1: From Small Drugs to Gene Editing
2022 Izzo, Mariapaola; Battistini, Jonathan; Provenzano, Claudia; Martelli, Fabio; Cardinali, Beatrice; Falcone, Germana
Gene Therapy Strategies For Myotonic Dystrophy Type 1
2021 Cardinali, Beatrice; Provenzano, Claudia; Izzo, Mariapaola; Battistini, Jonathan; Strimpakos, Georgios; Golini, Elisabetta; Mandillo, Silvia; Scavizzi, Ferdinando; Raspa, Marcello; Voellenkle, Christine; Perfetti, Alessandra; Baci, Denisa; Martelli, Fabio; Gourdon, Genevieve; Falcone, Germana
Inducible CRISPR/Cas9 strategy mediates efficient gene editing of trinucleotide repeat expansion in DMPK locus
2021 Cardinali, B; Provenzano, C; Izzo, Mariapaola; Voellenkle, C; Battistini, J; Strimpakos, G; Golini, E; Mandillo, S; Scavizzi, F; Raspa, M; Perfetti, A; Baci, D; Lazarevic, D; Garciamanteiga, J; F Martelli, G Gourdon; Falcone, G
Time-controlled and muscle-specific CRISPR/Cas9 mediated deletion of CTG-repeat expansion in the DMPK gene
2021 Cardinali, B; Provenzano, C; Izzo, M; Voellenkle, C; Battistini, J; Strimpakos, G; Golini, E; Mandillo, S; Scavizzi, F; Raspa, M; Perfetti, A; Baci, D; Lazarevic, D; Garciamanteiga, Jm; Gourdon, G; Martelli, F; Falcone, G
Circulating miRNAs in Small Extracellular Vesicles Secreted by a Human Melanoma Xenograft in Mouse Brains
2020 Guglielmi, Loredana; Nardella, Marta; Musa, Carla; Cifola, Ingrid; Porru, Manuela; Cardinali, Beatrice; Iannetti, Ilaria; DI PIETRO, Chiara; Bolasco, Giulia; Palmieri, Valentina; Vilardo, Laura; Panini, Nicolò; Bonaventura, Fabrizio; Papi, Massimiliano; Scavizzi, Ferdinando; Raspa, Marcello; Leonetti, Carlo; Falcone, Germana; Felsani, Armando; D'Agnano, Igea
Design of novel small molecule base-pair recognizers of toxic CUG RNA transcripts characteristics of DM1
2020 Ondono, Raul; Lirio, Ángel; Elvira, Carlos; Álvarezmarimon, Elena; Provenzano, Claudia; Cardinali, Beatrice; Pérezalonso, Manuel; Perálvarezmarín, Alex; I Borrell, José; Falcone, Germana; Estradatejedor, Roger
A new role of miR-29c as a potent inducer of skeletal muscle hypertrophy
2019 Falcone, Germana
Dysregulation of Circular RNAs in Myotonic Dystrophy Type 1
2019 Voellenkle, Christine; Perfetti, Alessandra; Carrara, Matteo; Fuschi, Paola; Valentina Renna, Laura; Longo, Marialucia; Baghai Sain, Simona; Cardani, Rosanna; Valaperta, Rea; Silvestri, Gabriella; Legnini, Ivano; Bozzoni, Irene; Furling, Denis; Gaetano, Carlo; Falcone, Germana; Meola, Giovanni; Martelli, Fabio
GENE EDITING IN MYOTONIC DYSTROPHY TYPE 1: ASSESSMENT OF EFFICIENCY, SAFETY AND THERAPEUTIC EFFECT OF CTG-REPEAT DELETION IN A MOUSE MODEL OF DISEASE
2019 Provenzano, C; Cardinali, B; Perfetti, A; Mandillo, S; Golini, E; Strimpakos, G; Voellenkle, C; Longo, M; Martelli, F; Falcone, G
| Titolo | Data di pubblicazione | Autore(i) | File |
|---|---|---|---|
| circARHGAP10 as a candidate biomarker and therapeutic target in myotonic dystrophy type 1 | 1-gen-2025 | Baci, D.; Tastsoglou, S.; Provenzano, C.; Perfetti, A.; Izzo, M.; Lisanti, M.; Frolova, S.; Voellenkle, C.; Tascini, A. S.; Cardani, R.; Cardinali, B.; Meola, G.; Falcone, G.; Martelli, F. | |
| Muscle‐specific gene editing improves molecular and phenotypic defects in a mouse model of myotonic dystrophy type 1 | 1-gen-2025 | Izzo, Mariapaola; Battistini, Jonathan; Golini, Elisabetta; Voellenkle, Christine; Provenzano, Claudia; Orsini, Tiziana; Strimpakos, Georgios; Scavizzi, Ferdinando; Raspa, Marcello; Baci, Denisa; Frolova, Svetlana; Tastsoglou, Spyros; Zaccagnini, Germana; Garcia‐manteiga, Jose Manuel; Gourdon, Genevieve; Mandillo, Silvia; Cardinali, Beatrice; Martelli, Fabio; Falcone, Germana | |
| Muscle-specific gene editing improves molecular and phenotypic defects in a mouse model of Myotonic Dystrophy type 1 | 1-gen-2024 | Izzo, Mariapaola; Battistini, Jonathan; Golini, Elisabetta; Provenzano, Claudia; Orsini, Tiziana; Strimpakos, Georgios; Scavizzi, Ferdinando; Raspa, Marcello; Gourdon, Genevieve; Mandillo, Silvia; Cardinali, Beatrice; Falcone, Germana | |
| Excessive rest time during active phase is reliably detected in a mouse model of myotonic dystrophy type 1 using home cage monitoring | 1-gen-2023 | Golini, Elisabetta; Rigamonti, Mara; Raspa, Marcello; Scavizzi, Ferdinando; Falcone, Germana; Gourdon, Genevieve; Mandillo, Silvia | |
| GENE EDITING IN MYOTONIC DYSTROPHY TYPE 1: ASSESSMENT OF EFFICIENCY, SAFETY AND THERAPEUTIC EFFECT OF CTG-REPEAT DELETION IN A MOUSE MODEL OF DISEASE | 1-gen-2023 | Izzo Mariapaola ; Battistini J.; Cardinali B.; Provenzano C.; Mandillo S.; Golini E.; Strimpakos G.; Scavizzi F.; Raspa M.; Voellenkle C.; Perfetti A.; Baci D.; Martelli F.; Lazarevic D.; GarciaManteiga J.M.; Gourdon G.; Falcone Germana | |
| Sleep-related phenotypes are non-invasively uncovered using home cage monitoring in mouse models of ALS and DM1 | 1-gen-2023 | Golini, Elisabetta; Rigamonti, Mara; Iannello, Fabio; Scavizzi, Ferdinando; Raspa, Marcello; Gourdon, Genevieve; Falcone, Germana; Mandillo, Silvia | |
| Study of pathogenetic mechanisms and development of new therapeutic strategies for Myotonic Dystrophy type 1 | 1-gen-2023 | M. Izzo ; J. Battistini ; B. Cardinali ; C. Provenzano ; S. Mandillo ; E. Golini ; G. Strimpakos ; F. Scavizzi ; M. Raspa ; C. Voellenkle ; D. Baci ; A. Perfetti ; D. Lazarevic ; J. GarciaManteiga ; G. Gourdon ; F. Martelli ; G. Falcone | |
| Application of CRISPR/Cas9 strategy for gene therapy of Myotonic Dystrophy type 1 | 1-gen-2022 | Falcone, G; Izzo, M; Cardinali, B; Provenzano, C; Battistini, J; Mandillo, S; Golini, E; Strimpakos, G; Scavizzi, F; Mraspa, ; Voellenkle, C; Baci, D; Perfetti, A; Lazarevic, D; Garciamanteiga, J; Gourdon, G; Martelli, F | |
| BEHAVIOURAL ABNORMALITIES IN DMSXL MICE, A MODEL OF MYOTONIC DYSTROPHY TYPE 1 | 1-gen-2022 | Mandillo, Silvia; Golini, Elisabetta; Orsini, Tiziana; Rigamonti, Mara; Izzo, Mariapaola; Battistini, Jonathan; Cardinali, Beatrice; Provenzano, Claudia; Strimpakos, Georgios; Scavizzi, Ferdinando; Raspa, Marcello; Genevievegourdon, ; Falcone, Germana | |
| Circular RNA role in Myotonic Dystrophy type 1 | 1-gen-2022 | Baci, D; Perfetti, A; Voellenkle, C; Cardani, R; Meola, G; Tascini, As; Provenzano, C; Cardinali, B; Falcone, G; Fmartelli, | |
| miRNome and Proteome Profiling of Small Extracellular Vesicles Secreted by Human Glioblastoma Cell Lines and Primary Cancer Stem Cells | 1-gen-2022 | Cifola, Ingrid; Fratini, Federica; Cardinali, Beatrice; Palmieri, Valentina; Gatti, Giuliana; Selmi, Tommaso; Donzelli, Sara; Sacconi, Andrea; Cesarini, Valeriana; E Marei, Hany; Papi, Massimilano; Blandino, Giovanni; Cenciarelli, Carlo; Falcone, Germana; D'Agnano, Igea | |
| Molecular Therapies for Myotonic Dystrophy Type 1: From Small Drugs to Gene Editing | 1-gen-2022 | Izzo, Mariapaola; Battistini, Jonathan; Provenzano, Claudia; Martelli, Fabio; Cardinali, Beatrice; Falcone, Germana | |
| Gene Therapy Strategies For Myotonic Dystrophy Type 1 | 1-gen-2021 | Cardinali, Beatrice; Provenzano, Claudia; Izzo, Mariapaola; Battistini, Jonathan; Strimpakos, Georgios; Golini, Elisabetta; Mandillo, Silvia; Scavizzi, Ferdinando; Raspa, Marcello; Voellenkle, Christine; Perfetti, Alessandra; Baci, Denisa; Martelli, Fabio; Gourdon, Genevieve; Falcone, Germana | |
| Inducible CRISPR/Cas9 strategy mediates efficient gene editing of trinucleotide repeat expansion in DMPK locus | 1-gen-2021 | Cardinali, B; Provenzano, C; Izzo, Mariapaola; Voellenkle, C; Battistini, J; Strimpakos, G; Golini, E; Mandillo, S; Scavizzi, F; Raspa, M; Perfetti, A; Baci, D; Lazarevic, D; Garciamanteiga, J; F Martelli, G Gourdon; Falcone, G | |
| Time-controlled and muscle-specific CRISPR/Cas9 mediated deletion of CTG-repeat expansion in the DMPK gene | 1-gen-2021 | Cardinali, B; Provenzano, C; Izzo, M; Voellenkle, C; Battistini, J; Strimpakos, G; Golini, E; Mandillo, S; Scavizzi, F; Raspa, M; Perfetti, A; Baci, D; Lazarevic, D; Garciamanteiga, Jm; Gourdon, G; Martelli, F; Falcone, G | |
| Circulating miRNAs in Small Extracellular Vesicles Secreted by a Human Melanoma Xenograft in Mouse Brains | 1-gen-2020 | Guglielmi, Loredana; Nardella, Marta; Musa, Carla; Cifola, Ingrid; Porru, Manuela; Cardinali, Beatrice; Iannetti, Ilaria; DI PIETRO, Chiara; Bolasco, Giulia; Palmieri, Valentina; Vilardo, Laura; Panini, Nicolò; Bonaventura, Fabrizio; Papi, Massimiliano; Scavizzi, Ferdinando; Raspa, Marcello; Leonetti, Carlo; Falcone, Germana; Felsani, Armando; D'Agnano, Igea | |
| Design of novel small molecule base-pair recognizers of toxic CUG RNA transcripts characteristics of DM1 | 1-gen-2020 | Ondono, Raul; Lirio, Ángel; Elvira, Carlos; Álvarezmarimon, Elena; Provenzano, Claudia; Cardinali, Beatrice; Pérezalonso, Manuel; Perálvarezmarín, Alex; I Borrell, José; Falcone, Germana; Estradatejedor, Roger | |
| A new role of miR-29c as a potent inducer of skeletal muscle hypertrophy | 1-gen-2019 | Falcone, Germana | |
| Dysregulation of Circular RNAs in Myotonic Dystrophy Type 1 | 1-gen-2019 | Voellenkle, Christine; Perfetti, Alessandra; Carrara, Matteo; Fuschi, Paola; Valentina Renna, Laura; Longo, Marialucia; Baghai Sain, Simona; Cardani, Rosanna; Valaperta, Rea; Silvestri, Gabriella; Legnini, Ivano; Bozzoni, Irene; Furling, Denis; Gaetano, Carlo; Falcone, Germana; Meola, Giovanni; Martelli, Fabio | |
| GENE EDITING IN MYOTONIC DYSTROPHY TYPE 1: ASSESSMENT OF EFFICIENCY, SAFETY AND THERAPEUTIC EFFECT OF CTG-REPEAT DELETION IN A MOUSE MODEL OF DISEASE | 1-gen-2019 | Provenzano, C; Cardinali, B; Perfetti, A; Mandillo, S; Golini, E; Strimpakos, G; Voellenkle, C; Longo, M; Martelli, F; Falcone, G |