FALCONE, GERMANA

FALCONE, GERMANA  

Istituto di Biochimica e Biologia Cellulare - IBBC  

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Excessive rest time during active phase is reliably detected in a mouse model of myotonic dystrophy type 1 using home cage monitoring 1-gen-2023 Golini, Elisabetta; Rigamonti, Mara; Raspa, Marcello; Scavizzi, Ferdinando; Falcone, Germana; Gourdon, Genevieve; Mandillo, Silvia
GENE EDITING IN MYOTONIC DYSTROPHY TYPE 1: ASSESSMENT OF EFFICIENCY, SAFETY AND THERAPEUTIC EFFECT OF CTG-REPEAT DELETION IN A MOUSE MODEL OF DISEASE 1-gen-2023 Izzo Mariapaola ; Battistini J.; Cardinali B.; Provenzano C.; Mandillo S.; Golini E.; Strimpakos G.; Scavizzi F.; Raspa M.; Voellenkle C.; Perfetti A.; Baci D.; Martelli F.; Lazarevic D.; GarciaManteiga J.M.; Gourdon G.; Falcone Germana
Sleep-related phenotypes are non-invasively uncovered using home cage monitoring in mouse models of ALS and DM1 1-gen-2023 Golini, Elisabetta; Rigamonti, Mara; Iannello, Fabio; Scavizzi, Ferdinando; Raspa, Marcello; Gourdon, Genevieve; Falcone, Germana; Mandillo, Silvia
Study of pathogenetic mechanisms and development of new therapeutic strategies for Myotonic Dystrophy type 1 1-gen-2023 M. Izzo ; J. Battistini ; B. Cardinali ; C. Provenzano ; S. Mandillo ; E. Golini ; G. Strimpakos ; F. Scavizzi ; M. Raspa ; C. Voellenkle ; D. Baci ; A. Perfetti ; D. Lazarevic ; J. GarciaManteiga ; G. Gourdon ; F. Martelli ; G. Falcone
Application of CRISPR/Cas9 strategy for gene therapy of Myotonic Dystrophy type 1 1-gen-2022 Falcone, G; Izzo, M; Cardinali, B; Provenzano, C; Battistini, J; Mandillo, S; Golini, E; Strimpakos, G; Scavizzi, F; Mraspa, ; Voellenkle, C; Baci, D; Perfetti, A; Lazarevic, D; Garciamanteiga, J; Gourdon, G; Martelli, F
BEHAVIOURAL ABNORMALITIES IN DMSXL MICE, A MODEL OF MYOTONIC DYSTROPHY TYPE 1 1-gen-2022 Mandillo, Silvia; Golini, Elisabetta; Orsini, Tiziana; Rigamonti, Mara; Izzo, Mariapaola; Battistini, Jonathan; Cardinali, Beatrice; Provenzano, Claudia; Strimpakos, Georgios; Scavizzi, Ferdinando; Raspa, Marcello; Genevievegourdon, ; Falcone, Germana
Circular RNA role in Myotonic Dystrophy type 1 1-gen-2022 Baci, D; Perfetti, A; Voellenkle, C; Cardani, R; Meola, G; Tascini, As; Provenzano, C; Cardinali, B; Falcone, G; Fmartelli,
miRNome and Proteome Profiling of Small Extracellular Vesicles Secreted by Human Glioblastoma Cell Lines and Primary Cancer Stem Cells 1-gen-2022 Cifola, Ingrid; Fratini, Federica; Cardinali, Beatrice; Palmieri, Valentina; Gatti, Giuliana; Selmi, Tommaso; Donzelli, Sara; Sacconi, Andrea; Cesarini, Valeriana; E Marei, Hany; Papi, Massimilano; Blandino, Giovanni; Cenciarelli, Carlo; Falcone, Germana; D'Agnano, Igea
Molecular Therapies for Myotonic Dystrophy Type 1: From Small Drugs to Gene Editing 1-gen-2022 Izzo, Mariapaola; Battistini, Jonathan; Provenzano, Claudia; Martelli, Fabio; Cardinali, Beatrice; Falcone, Germana
Gene Therapy Strategies For Myotonic Dystrophy Type 1 1-gen-2021 Cardinali, Beatrice; Provenzano, Claudia; Izzo, Mariapaola; Battistini, Jonathan; Strimpakos, Georgios; Golini, Elisabetta; Mandillo, Silvia; Scavizzi, Ferdinando; Raspa, Marcello; Voellenkle, Christine; Perfetti, Alessandra; Baci, Denisa; Martelli, Fabio; Gourdon, Genevieve; Falcone, Germana
Inducible CRISPR/Cas9 strategy mediates efficient gene editing of trinucleotide repeat expansion in DMPK locus 1-gen-2021 Cardinali, B; Provenzano, C; Izzo, Mariapaola; Voellenkle, C; Battistini, J; Strimpakos, G; Golini, E; Mandillo, S; Scavizzi, F; Raspa, M; Perfetti, A; Baci, D; Lazarevic, D; Garciamanteiga, J; F Martelli, G Gourdon; Falcone, G
Time-controlled and muscle-specific CRISPR/Cas9 mediated deletion of CTG-repeat expansion in the DMPK gene 1-gen-2021 Cardinali, B; Provenzano, C; Izzo, M; Voellenkle, C; Battistini, J; Strimpakos, G; Golini, E; Mandillo, S; Scavizzi, F; Raspa, M; Perfetti, A; Baci, D; Lazarevic, D; Garciamanteiga, Jm; Gourdon, G; Martelli, F; Falcone, G
Circulating miRNAs in Small Extracellular Vesicles Secreted by a Human Melanoma Xenograft in Mouse Brains 1-gen-2020 Guglielmi, Loredana; Nardella, Marta; Musa, Carla; Cifola, Ingrid; Porru, Manuela; Cardinali, Beatrice; Iannetti, Ilaria; DI PIETRO, Chiara; Bolasco, Giulia; Palmieri, Valentina; Vilardo, Laura; Panini, Nicolò; Bonaventura, Fabrizio; Papi, Massimiliano; Scavizzi, Ferdinando; Raspa, Marcello; Leonetti, Carlo; Falcone, Germana; Felsani, Armando; D'Agnano, Igea
Design of novel small molecule base-pair recognizers of toxic CUG RNA transcripts characteristics of DM1 1-gen-2020 Ondono, Raul; Lirio, Ángel; Elvira, Carlos; Álvarezmarimon, Elena; Provenzano, Claudia; Cardinali, Beatrice; Pérezalonso, Manuel; Perálvarezmarín, Alex; I Borrell, José; Falcone, Germana; Estradatejedor, Roger
A new role of miR-29c as a potent inducer of skeletal muscle hypertrophy 1-gen-2019 Falcone, Germana
Dysregulation of Circular RNAs in Myotonic Dystrophy Type 1 1-gen-2019 Voellenkle, Christine; Perfetti, Alessandra; Carrara, Matteo; Fuschi, Paola; Valentina Renna, Laura; Longo, Marialucia; Baghai Sain, Simona; Cardani, Rosanna; Valaperta, Rea; Silvestri, Gabriella; Legnini, Ivano; Bozzoni, Irene; Furling, Denis; Gaetano, Carlo; Falcone, Germana; Meola, Giovanni; Martelli, Fabio
GENE EDITING IN MYOTONIC DYSTROPHY TYPE 1: ASSESSMENT OF EFFICIENCY, SAFETY AND THERAPEUTIC EFFECT OF CTG-REPEAT DELETION IN A MOUSE MODEL OF DISEASE 1-gen-2019 Provenzano, C; Cardinali, B; Perfetti, A; Mandillo, S; Golini, E; Strimpakos, G; Voellenkle, C; Longo, M; Martelli, F; Falcone, G
Circular RNAs in muscle function and disease 1-gen-2018 Greco, Simona; Cardinali, Beatrice; Falcone, Germana; Martelli, Fabio
High-throughput analysis of the RNAinduced silencing complex in myotonic dystrophy type 1 patients identifies the dysregulation of miR-29c and its target ASB2 1-gen-2018 Cappella, Marisa; Perfetti, Alessandra; Cardinali, Beatrice; GarciaManteiga Jose, Manuel; Carrara, Matteo; Provenzano, Claudia; Fuschi, Paola; Cardani, Rosanna; Renna Laura, Valentina; Meola, Giovanni; Falcone, Germana; Martelli, Fabio
CRISPR/Cas9-MediatedDeletion ofCTGExpansions Recovers Normal Phenotype in Myogenic Cells Derived from Myotonic Dystrophy 1 Patients 1-gen-2017 Provenzano, Claudia; Cappella, Marisa; Valaperta, Rea; Cardani, Rosanna; Meola, Giovanni; Martelli Beatrice Cardinali, Fabio; Falcone, Germana