PROVENZANO, CLAUDIA

PROVENZANO, CLAUDIA  

Istituto di Biochimica e Biologia Cellulare - IBBC  

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Titolo Data di pubblicazione Autore(i) File
GENE EDITING IN MYOTONIC DYSTROPHY TYPE 1: ASSESSMENT OF EFFICIENCY, SAFETY AND THERAPEUTIC EFFECT OF CTG-REPEAT DELETION IN A MOUSE MODEL OF DISEASE 1-gen-2023 Izzo Mariapaola ; Battistini J.; Cardinali B.; Provenzano C.; Mandillo S.; Golini E.; Strimpakos G.; Scavizzi F.; Raspa M.; Voellenkle C.; Perfetti A.; Baci D.; Martelli F.; Lazarevic D.; GarciaManteiga J.M.; Gourdon G.; Falcone Germana
Study of pathogenetic mechanisms and development of new therapeutic strategies for Myotonic Dystrophy type 1 1-gen-2023 M. Izzo ; J. Battistini ; B. Cardinali ; C. Provenzano ; S. Mandillo ; E. Golini ; G. Strimpakos ; F. Scavizzi ; M. Raspa ; C. Voellenkle ; D. Baci ; A. Perfetti ; D. Lazarevic ; J. GarciaManteiga ; G. Gourdon ; F. Martelli ; G. Falcone
Application of CRISPR/Cas9 strategy for gene therapy of Myotonic Dystrophy type 1 1-gen-2022 Falcone, G; Izzo, M; Cardinali, B; Provenzano, C; Battistini, J; Mandillo, S; Golini, E; Strimpakos, G; Scavizzi, F; Mraspa, ; Voellenkle, C; Baci, D; Perfetti, A; Lazarevic, D; Garciamanteiga, J; Gourdon, G; Martelli, F
BEHAVIOURAL ABNORMALITIES IN DMSXL MICE, A MODEL OF MYOTONIC DYSTROPHY TYPE 1 1-gen-2022 Mandillo, Silvia; Golini, Elisabetta; Orsini, Tiziana; Rigamonti, Mara; Izzo, Mariapaola; Battistini, Jonathan; Cardinali, Beatrice; Provenzano, Claudia; Strimpakos, Georgios; Scavizzi, Ferdinando; Raspa, Marcello; Genevievegourdon, ; Falcone, Germana
Circular RNA role in Myotonic Dystrophy type 1 1-gen-2022 Baci, D; Perfetti, A; Voellenkle, C; Cardani, R; Meola, G; Tascini, As; Provenzano, C; Cardinali, B; Falcone, G; Fmartelli,
Molecular Therapies for Myotonic Dystrophy Type 1: From Small Drugs to Gene Editing 1-gen-2022 Izzo, Mariapaola; Battistini, Jonathan; Provenzano, Claudia; Martelli, Fabio; Cardinali, Beatrice; Falcone, Germana
Gene Therapy Strategies For Myotonic Dystrophy Type 1 1-gen-2021 Cardinali, Beatrice; Provenzano, Claudia; Izzo, Mariapaola; Battistini, Jonathan; Strimpakos, Georgios; Golini, Elisabetta; Mandillo, Silvia; Scavizzi, Ferdinando; Raspa, Marcello; Voellenkle, Christine; Perfetti, Alessandra; Baci, Denisa; Martelli, Fabio; Gourdon, Genevieve; Falcone, Germana
Inducible CRISPR/Cas9 strategy mediates efficient gene editing of trinucleotide repeat expansion in DMPK locus 1-gen-2021 Cardinali, B; Provenzano, C; Izzo, Mariapaola; Voellenkle, C; Battistini, J; Strimpakos, G; Golini, E; Mandillo, S; Scavizzi, F; Raspa, M; Perfetti, A; Baci, D; Lazarevic, D; Garciamanteiga, J; F Martelli, G Gourdon; Falcone, G
Time-controlled and muscle-specific CRISPR/Cas9 mediated deletion of CTG-repeat expansion in the DMPK gene 1-gen-2021 Cardinali, B; Provenzano, C; Izzo, M; Voellenkle, C; Battistini, J; Strimpakos, G; Golini, E; Mandillo, S; Scavizzi, F; Raspa, M; Perfetti, A; Baci, D; Lazarevic, D; Garciamanteiga, Jm; Gourdon, G; Martelli, F; Falcone, G
Design of novel small molecule base-pair recognizers of toxic CUG RNA transcripts characteristics of DM1 1-gen-2020 Ondono, Raul; Lirio, Ángel; Elvira, Carlos; Álvarezmarimon, Elena; Provenzano, Claudia; Cardinali, Beatrice; Pérezalonso, Manuel; Perálvarezmarín, Alex; I Borrell, José; Falcone, Germana; Estradatejedor, Roger
GENE EDITING IN MYOTONIC DYSTROPHY TYPE 1: ASSESSMENT OF EFFICIENCY, SAFETY AND THERAPEUTIC EFFECT OF CTG-REPEAT DELETION IN A MOUSE MODEL OF DISEASE 1-gen-2019 Provenzano, C; Cardinali, B; Perfetti, A; Mandillo, S; Golini, E; Strimpakos, G; Voellenkle, C; Longo, M; Martelli, F; Falcone, G
High-throughput analysis of the RNAinduced silencing complex in myotonic dystrophy type 1 patients identifies the dysregulation of miR-29c and its target ASB2 1-gen-2018 Cappella, Marisa; Perfetti, Alessandra; Cardinali, Beatrice; GarciaManteiga Jose, Manuel; Carrara, Matteo; Provenzano, Claudia; Fuschi, Paola; Cardani, Rosanna; Renna Laura, Valentina; Meola, Giovanni; Falcone, Germana; Martelli, Fabio
CRISPR/Cas9-MediatedDeletion ofCTGExpansions Recovers Normal Phenotype in Myogenic Cells Derived from Myotonic Dystrophy 1 Patients 1-gen-2017 Provenzano, Claudia; Cappella, Marisa; Valaperta, Rea; Cardani, Rosanna; Meola, Giovanni; Martelli Beatrice Cardinali, Fabio; Falcone, Germana
MicroRNA-222 regulates muscle alternative splicing through Rbm24 during differentiation of skeletal muscle cells 1-gen-2016 Cardinali B; Cappella M; Provenzano C; GarciaManteiga JM; Lazarevic D; Cittaro D; Martelli F; Falcone G.
MiR-21 is an Ngf-modulated MicroRNA That supports Ngf signaling and regulates neuronal degeneration in PC12 cells 1-gen-2014 Montalban, E; Mattugini, N; Ciarapica, R; Provenzano, C; Savino, M; Scagnoli, F; Prosperini, G; Carissimi, C; Fulci, V; Matrone, C; Calissano, P; Nasi, S
Does the term 'trophic' actually mean anti-amyloidogenic? The case of NGF 1-gen-2010 Calissano, P; Amadoro, G; Matrone, C; Ciafrè, S; Marolda, R; Corsetti, V; Ciotti, Mt; Mercanti, D; Di Luzio, A; Severini, C; Provenzano, C; Canu, N
Large scale analysis of transcription factor TTF-1/NKX2.1 target genes in GnRH secreting cell line GT1-7 1-gen-2010 Provenzano, C; Pascucci, B; Lupari, E; Civitareale, D
Functional characterization of a novel mutations in TITF-1 in a patient with Benign Hereditary Chorea. 1-gen-2007 Veneziano, L; Provenzano, C; Mantuano, E; Guida, S; Appleton, R; Frontali, M; Civitareale, D
Retinoblastoma protein acts as Pax 8 transcriptional coactivator. 1-gen-2005 Miccadei S.; Provenzano C.; Mojzisek M.; Natali P.G.; Civitareale D..
v-Src inhibits myogenic differentiation by interfering with the regulatory network of muscle-specific transcriptional activators at multiple levels 1-gen-2003 Falcone G.; Ciuffini L.; Gauzzi M.C.; Provenzano C.; Strano S.; Castellani L.;Alemà S